First experience of combined enzyme replacement therapy and hematopoietic stem cell transplantation in alpha-mannosidosis.
Santoro L, Monachesi C, Zampini L, Padella L, Galeazzi T, Santori E, Cordiali R, Dardis A, Catassi C, Boccieri E, et al. First experience of combined enzyme replacement therapy and hematopoietic stem cell transplantation in alpha-mannosidosis. Am J Med Genet A. 2023.