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Donsante S, Pievani A, Palmisano B, Finamore M, Fazio G, Corsi A, Biondi A, Tomatsu S, Piazza R, Serafini M, et al. Modeling skeletal dysplasia in Hurler syndrome using patient-derived bone marrow osteoprogenitor cells. JCI Insight. 2024;9(5).