Biblio
Genome engineering of a neuronal specific, optogenetic, induced pluripotent stem cell line. Stem Cell Res. 2024;75:103317.
. Preclinical evaluation of CRISPR-based therapies for Noonan syndrome caused by deep-intronic variants. Mol Ther Nucleic Acids. 2024;35(1):102123.
. Protocol to develop force-generating human skeletal muscle organoids. STAR Protoc. 2023;5(1):102794.
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19 Annual Meeting of the Safety Pharmacology Society: regulatory and safety perspectives for advanced therapy medicinal products (cellular and gene therapy products). Expert Opin Drug Saf. 2020.
. Challenges to Heart Repair with Pluripotent Stem Cell-Derived Cardiomyocytes. Trends Cardiovasc Med. 2020.
. Generation of homozygous CRISPRa human induced pluripotent stem cell (hiPSC) lines for sustained endogenous gene activation. Stem Cell Res. 2020;48:101944.
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Cardiac Engraftment of Genetically-Selected Parthenogenetic Stem Cell-Derived Cardiomyocytes. PLoS One. 2015;10(6):e0131511.
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