Biblio
[Establishment of hemophilia A patient-specific inducible pluripotent stem cells with urine cells]. Zhonghua Yi Xue Yi Chuan Xue Za Zhi. 2015;32(5):609-614.
. ssODN-Mediated In-Frame Deletion with CRISPR/Cas9 Restores FVIII Function in Hemophilia A-Patient-Derived iPSCs and ECs. Mol Ther Nucleic Acids. 2019;17:198-209.
. Targeted addition of mini-dystrophin into rDNA locus of Duchenne muscular dystrophy patient-derived iPSCs. Biochem Biophys Res Commun. 2021;545:40-45.
Targeting of the Human F8 at the Multicopy rDNA Locus in Hemophilia A Patient-Derived iPSCs Using TALENickases. Biochem Biophys Res Commun. 2016.