Biblio
Author Title Type [ Year]
Filters: First Letter Of Title is S and Author is Schmidt, Iris [Clear All Filters]
Splice-Modulating Oligonucleotide QR-110 Restores CEP290 mRNA and Function in Human c.2991+1655A>G LCA10 Models. Mol Ther Nucleic Acids. 2018;12:730-740.