Biblio

Author Title Type [ Year(Desc)]
Filters: Author is Ferrua, Francesca  [Clear All Filters]
2019
Bortolomai I, Sandri M, Draghici E, Fontana E, Campodoni E, Marcovecchio GEnza, Ferrua F, Perani L, Spinelli A, Canu T, et al. Gene Modification and Three-Dimensional Scaffolds as Novel Tools to Allow the Use of Postnatal Thymic Epithelial Cells for Thymus Regeneration Approaches. Stem Cells Transl Med. 2019.
Ferrua F, Galimberti S, Courteille V, Slatter MAnne, Booth C, Moshous D, Neven B, Blanche S, Laberko A, Shcherbina A, et al. Hematopoietic stem cell transplantation for CD40 ligand deficiency: results from an EBMT/ESID-IEWP-SCETIDE-PIDTC Study. J Allergy Clin Immunol. 2019.
Ferrua F, Cicalese MPia, Galimberti S, Giannelli S, Dionisio F, Barzaghi F, Migliavacca M, Bernardo MEster, Calbi V, Assanelli AAngelo, et al. Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study. Lancet Haematol. 2019.
2020
Ferrua F, Marangoni F, Aiuti A, Roncarolo MGrazia. Gene Therapy for Wiskott-Aldrich Syndrome: History, New Vectors, Future Directions. J Allergy Clin Immunol. 2020.
2021
Consiglieri G, Ferrua F, Aiuti A, Cicalese MPia. A Case of Two Adult Brothers with Wiskott-Aldrich Syndrome, One Treated with Gene Therapy and One with HLA-Identical Hematopoietic Stem Cell Transplantation. J Clin Immunol. 2021.
Gentner B, Tucci F, Galimberti S, Fumagalli F, De Pellegrin M, Silvani P, Camesasca C, Pontesilli S, Darin S, Ciotti F, et al. Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome. N Engl J Med. 2021;385(21):1929-1940.
2023
Scala S, Ferrua F, Basso-Ricci L, Dionisio F, Omrani M, Quaranta P, Hernández RJofra, Del Core L, Benedicenti F, Monti I, et al. Hematopoietic reconstitution dynamics of mobilized- and bone marrow-derived human hematopoietic stem cells after gene therapy. Nat Commun. 2023;14(1):3068.
Fratini ESophia, Migliavacca M, Barzaghi F, Fossati C, Giannelli S, Monti I, Casiraghi M, Ferrua F, Recupero S, Consiglieri G, et al. Hemophagocytic inflammatory syndrome in ADA-SCID: report of two cases and literature review. Front Immunol. 2023;14:1187959.
Asperti C, Canarutto D, Porcellini S, Sanvito F, Cecere F, Vavassori V, Ferrari S, Rovelli E, Albano L, Jacob A, et al. Scalable GMP-compliant gene correction of CD4+ T cells with IDLV template functionally validated and . Mol Ther Methods Clin Dev. 2023;30:546-557.
2024
Quaranta P, Basso-Ricci L, Hernández RJofra Jofr, Pacini G, Naldini MMaria, Barcella M, Seffin L, Pais G, Spinozzi G, Benedicenti F, et al. Circulating Hematopoietic Stem/Progenitor Cells subsets contribute to human hematopoietic homeostasis. Blood. 2024.
Consiglieri G, Tucci F, De Pellegrin M, Guerrini B, Cattoni A, Risca G, Scarparo S, Sarzana M, Pontesilli S, Mellone R, et al. Early skeletal outcomes after hematopoietic stem and progenitor cell gene therapy for Hurler syndrome. Sci Transl Med. 2024;16(745):eadi8214.
Vallée TC, Glasmacher JS, Buchner H, Arkwright PD, Behrends U, Bondarenko A, Browning MJ, Buchbinder DK, Cattoni A, Chernyshova L, et al. Wiskott-Aldrich Syndrome: A study on 577 patients defining the genotype as a predictive biomarker for disease severity. Blood. 2024.