Biblio

Author Title [ Type(Desc)] Year
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Journal Article
Chen PP, Cepika A-M, Agarwal-Hashmi R, Saini G, Uyeda MJ, Louis DM, Cieniewicz B, Narula M, Hernandez LCAmaya, Harre N, et al. Alloantigen-specific type 1 regulatory T cells suppress through CTLA-4 and PD-1 pathways and persist long-term in patients. Sci Transl Med. 2021;13(617):eabf5264.
Roncarolo MGrazia, Gregori S, Bacchetta R, Battaglia M, Gagliani N. The Biology of T Regulatory Type 1 Cells and Their Therapeutic Application in Immune-Mediated Diseases. Immunity. 2018;49(6):1004-1019.
Wilkes MC, Scanlon V, Shibuya A, Celika A-M, Eskin A, Chen Z, Narla A, Glader B, Roncarolo MGrazia, Nelson SF, et al. Downregulation of SATB1 by miRNAs Reduces Megakaryocyte/Erythroid Progenitor Expansion in pre-clinical models of Diamond Blackfan Anemia. Exp Hematol. 2022.
Ferrua F, Marangoni F, Aiuti A, Roncarolo MGrazia. Gene Therapy for Wiskott-Aldrich Syndrome: History, New Vectors, Future Directions. J Allergy Clin Immunol. 2020.
Borna S, Lee E, Nideffer J, Ramachandran A, Wang B, Baker J, Mavers M, Lakshmanan U, Narula M, Garrett AKang-Hee, et al. Identification of unstable regulatory and autoreactive effector T cells that are expanded in patients with mutations. Sci Transl Med. 2023;15(727):eadg6822.
Bacchetta R, Roncarolo MGrazia. IPEX Syndrome from diagnosis to cure, learning along the way. J Allergy Clin Immunol. 2023.
Sessa M, Lorioli L, Fumagalli F, Acquati S, Redaelli D, Baldoli C, Canale S, Lopez ID, Morena F, Calabria A, et al. Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial. Lancet. 2016.
Ferrua F, Cicalese MPia, Galimberti S, Giannelli S, Dionisio F, Barzaghi F, Migliavacca M, Bernardo MEster, Calbi V, Assanelli AAngelo, et al. Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study. Lancet Haematol. 2019.
Brockmann L, Soukou S, Steglich B, Czarnewski P, Zhao L, Wende S, Bedke T, Ergen C, Manthey C, Agalioti T, et al. Molecular and functional heterogeneity of IL-10-producing CD4 T cells. Nat Commun. 2018;9(1):5457.
Roth TL, Puig-Saus C, Yu R, Shifrut E, Carnevale J, P Li J, Hiatt J, Saco J, Krystofinski P, Li H, et al. Reprogramming human T cell function and specificity with non-viral genome targeting. Nature. 2018.