Biblio
Alloantigen-specific type 1 regulatory T cells suppress through CTLA-4 and PD-1 pathways and persist long-term in patients. Sci Transl Med. 2021;13(617):eabf5264.
The Biology of T Regulatory Type 1 Cells and Their Therapeutic Application in Immune-Mediated Diseases. Immunity. 2018;49(6):1004-1019.
. Downregulation of SATB1 by miRNAs Reduces Megakaryocyte/Erythroid Progenitor Expansion in pre-clinical models of Diamond Blackfan Anemia. Exp Hematol. 2022.
Gene Therapy for Wiskott-Aldrich Syndrome: History, New Vectors, Future Directions. J Allergy Clin Immunol. 2020.
. Identification of unstable regulatory and autoreactive effector T cells that are expanded in patients with mutations. Sci Transl Med. 2023;15(727):eadg6822.
IPEX Syndrome from diagnosis to cure, learning along the way. J Allergy Clin Immunol. 2023.
. Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study. Lancet Haematol. 2019.
Molecular and functional heterogeneity of IL-10-producing CD4 T cells. Nat Commun. 2018;9(1):5457.