Biblio
A universal gene correction approach for FKRP-associated dystroglycanopathies to enable autologous cell therapy. Cell Rep. 2021;36(2):109360.
Transplantation studies reveal internuclear transfer of toxic RNA in engrafted muscles of myotonic dystrophy 1 mice. EBioMedicine. 2019.
. Time-dependent Pax3-mediated chromatin remodeling and cooperation with Six4 and Tead2 specify the skeletal myogenic lineage in developing mesoderm. PLoS Biol. 2019;17(2):e3000153.
Skeletal Muscle Stem Cells from PSC-Derived Teratomas Have Functional Regenerative Capacity. Cell Stem Cell. 2018;23(1):74-85.e6.
. Proliferation and Maturation: Janus and the Art of Cardiac Tissue Engineering. Circ Res. 2023;132(4):519-540.
. Pluripotent Stem Cell-Based Therapeutics for Muscular Dystrophies. Trends Mol Med. 2019.
. Pax3 and Tbx5 specify whether PDGFRα+ cells assume skeletal or cardiac muscle fate in differentiating ES cells. Stem Cells. 2014.
. Nanotopography-responsive myotube alignment and orientation as a sensitive phenotypic biomarker for Duchenne Muscular Dystrophy. Biomaterials. 2018;183:54-66.
. In vitro expanded skeletal myogenic progenitors from pluripotent stem cell-derived teratomas have high engraftment capacity. Stem Cell Reports. 2021.
. Genomic Safe Harbor Expression of PAX7 for the Generation of Engraftable Myogenic Progenitors. Stem Cell Reports. 2020.
. Expression levels of Endoglin Distinctively Identify Hematopoietic and Endothelial Progeny at Different Stages of Yolk Sac Hematopoiesis. Stem Cells. 2013.
. Development of allogeneic iPS cell-based therapy: from bench to bedside. EMBO Mol Med. 2022:e15315.
. Defective autophagy and increased apoptosis contribute toward the pathogenesis of FKRP-associated muscular dystrophies. Stem Cell Reports. 2021.
. Chromatin accessibility profiling identifies evolutionary conserved loci in activated human satellite cells. Stem Cell Res. 2021;55:102496.
. The adult environment promotes the transcriptional maturation of human iPSC-derived muscle grafts. NPJ Regen Med. 2024;9(1):16.
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