Biblio
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Eye on a Dish Models to Evaluate Splicing Modulation. Methods Mol Biol. 2022;2434:245-255.
. Modeling and Rescue of RP2 Retinitis Pigmentosa Using iPSC-Derived Retinal Organoids. Stem Cell Reports. 2020.
Splice-Modulating Oligonucleotide QR-110 Restores CEP290 mRNA and Function in Human c.2991+1655A>G LCA10 Models. Mol Ther Nucleic Acids. 2018;12:730-740.
Using Stem Cells to Model Diseases of the Outer Retina. Comput Struct Biotechnol J. 2015;13:382-9.
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