Biblio
2021
Risitano AM, Röth A, Soret J, Frieri C, de Fontbrune FSicre, Marano L, Alashkar F, Benajiba L, Marotta S, Rozenberg I, et al. Addition of iptacopan, an oral factor B inhibitor, to eculizumab in patients with paroxysmal nocturnal haemoglobinuria and active haemolysis: an open-label, single-arm, phase 2, proof-of-concept trial. Lancet Haematol. 2021.