Biblio
2021
Ramírez MJosé, Pujol R, Trujillo-Quintero JPablo, Minguillón J, Bogliolo M, Rio P, Navarro S, Casado JA, Badell I, Carrasco E, et al. Natural gene therapy by reverse mosaicism leads to improved hematology in Fanconi anemia patients. Am J Hematol. 2021.