Biblio
Severe combined immunodeficiency: improved survival leading to detection of underlying liver disease. BMC Gastroenterol. 2023;23(1):166.
. Morbidity, Mortality, and Therapeutics in Combined Immunodeficiency: Data from the USIDNET Registry. J Allergy Clin Immunol Pract. 2022.
. Clinical Manifestations and Outcomes of Activated Phosphoinositide 3-Kinase δ Syndrome from the USIDNET Cohort. J Allergy Clin Immunol Pract. 2021.
. Busulfan Pharmacokinetics in ADA SCID Gene Therapy. Biol Blood Marrow Transplant. 2020.
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