Biblio
Small-Molecule PAPD5 Inhibitors Restore Telomerase Activity in Patient Stem Cells. Cell Stem Cell. 2020.
Rational targeting of a NuRD subcomplex guided by comprehensive in situ mutagenesis. Nat Genet. 2019.
Genome editing of HBG1 and HBG2 to induce fetal hemoglobin. Blood Adv. 2019;3(21):3379-3392.
Enhanced Cas12a editing in mammalian cells and zebrafish. Nucleic Acids Res. 2019.
Dissecting ELANE neutropenia pathogenicity by human HSC gene editing. Cell Stem Cell. 2021.