Biblio
Diagnosis and treatment of pediatric acquired aplastic anemia (AAA): An initial survey of the North American Pediatric Aplastic Anemia Consortium (NAPAAC). Pediatr Blood Cancer. 2013.
Investigational curative gene therapy approaches to sickle cell disease. Blood Adv. 2021;5(23):5452.
. The long road traveled in hematopoietic stem cell gene therapy. Mol Ther. 2022.
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