Biblio
Pre-hematopoietic stem cell transplant lung function and pulmonary complications in children. Ann Am Thorac Soc. 2014.
. Potent and uniform fetal hemoglobin induction via base editing. Nat Genet. 2023.
Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1. N Engl J Med. 2019;380(16):1525-1534.
Impact of Adenoviral Stool Load on Adenoviremia in Pediatric Hematopoietic Stem Cell Transplant Recipients. Pediatr Infect Dis J. 2015.
. IL-13/IL-4 signaling contributes to fibrotic progression of the myeloproliferative neoplasms. Blood. 2022.
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