Biblio
2019
Marktel, S., Scaramuzza, S., Cicalese, M.Pia, Giglio, F., Galimberti, S., Lidonnici, M.Rosa, Calbi, V., Assanelli, A., Bernardo, M.Ester, Rossi, C., et al. (2019).
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia.Nat Med.
Ferrua, F., Cicalese, M.Pia, Galimberti, S., Giannelli, S., Dionisio, F., Barzaghi, F., Migliavacca, M., Bernardo, M.Ester, Calbi, V., Assanelli, A.Angelo, et al. (2019).
Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study.Lancet Haematol.