Biblio
Production and First-in-Man Use of T Cells Engineered to Express a HSVTK-CD34 Sort-Suicide Gene. PLoS One. 2013;8(10):e77106.
Outcomes Following Gene Therapy in Patients With Severe Wiskott-Aldrich Syndrome. JAMA. 2015;313(15):1550-1563.
Dysmorphism and immunodeficiency - One of the differential diagnoses is PAX1 related otofaciocervical syndrome type 2. Eur J Med Genet. 2022:104523.
. Base-Edited CAR7 T Cells for Relapsed T-Cell Acute Lymphoblastic Leukemia. N Engl J Med. 2023.
Fevers and ulcers in a newborn-Think genetics and act quickly. Pediatr Allergy Immunol. 2024;35(3):e14102.
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