Biblio

Author Title [ Type(Desc)] Year
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Journal Article
Pinello, L., Canver, M.C., Hoban, M.D., Orkin, S.H., Kohn, D.B., Bauer, D.E., and Yuan, G.-C. (2016). Analyzing CRISPR genome-editing experiments with CRISPResso.Nat Biotechnol34, 695-697.
Kohn, D.B., Hershfield, M.S., Puck, J.M., Aiuti, A., Blincoe, A., H Gaspar, B., Notarangelo, L.D., and Grunebaum, E. (2018). Consensus approach for the management of severe combined immune deficiency caused by adenosine deaminase deficiency.J Allergy Clin Immunol.
Kohn, D.B. (2014). Eliminating SCID row: new approaches to SCID.Hematology Am Soc Hematol Educ Program2014, 475-480.
Kohn, D.B. (2018). Gene therapy for blood diseases.Curr Opin Biotechnol60, 39-45.
Gschweng, E.H., McCracken, M.N., Kaufman, M.L., Ho, M., Hollis, R.P., Wang, X., Saini, N., Koya, R.C., Chodon, T., Ribas, A., et al. (2014). HSV-sr39TK positron emission tomography and suicide gene elimination of human hematopoietic stem cells and their progeny in humanized mice.Cancer Res.
Lomova, A., Clark, D.N., Campo-Fernandez, B., Flores-Bjurström, C., Kaufman, M.L., Fitz-Gibbon, S., Wang, X., Miyahira, E.Y., Brown, D., DeWitt, M.A., et al. (2018). Improving Gene Editing Outcomes in Human Hematopoietic Stem and Progenitor Cells by Temporal Control of DNA Repair.Stem Cells.
Joglekar, A.V., Hollis, R.P., Kuftinec, G., Senadheera, S., Chan, R., and Kohn, D.B. (2013). Integrase-defective Lentiviral Vectors as a Delivery Platform for Targeted Modification of Adenosine Deaminase Locus.Mol Ther.
Punwani, D., Kawahara, M., Yu, J., Sanford, U., Roy, S., Patel, K., Carbonaro, D.A., Karlen, A.D., Khan, S., Cornetta, K.G., et al. (2016). Lentivirus Mediated Correction of Artemis-deficient Severe Combined Immunodeficiency.Hum Gene Ther.
Urbinati, F., Hargrove, P.W., Geiger, S., Romero, Z., Wherley, J., Kaufman, M.L., Hollis, R.P., Chambers, C.B., Persons, D.A., Kohn, D.B., et al. (2015). Potentially Therapeutic Levels of Anti-Sickling Globin Gene Expression Following Lentivirus-mediated Gene Transfer in Sickle Cell Disease Bone Marrow CD34(+)Cells.Exp Hematol.
Griffith, L.M., Cowan, M.J., Notarangelo, L.D., Kohn, D.B., Puck, J.M., Shearer, W.T., Burroughs, L.M., Torgerson, T.R., Decaluwe, H., and Haddad, E. (2016). Primary Immune Deficiency Treatment Consortium (PIDTC) update.J Allergy Clin Immunol.
Stoyanova, T., Cooper, A.R., Drake, J.M., Liu, X., Armstrong, A.J., Pienta, K.J., Zhang, H., Kohn, D.B., Huang, J., Witte, O.N., et al. (2013). Prostate cancer originating in basal cells progresses to adenocarcinoma propagated by luminal-like cells.Proc Natl Acad Sci U S A.