Biblio
Adenosine Deaminase (ADA)-Deficient Severe Combined Immune Deficiency (SCID) in the US Immunodeficiency Network (USIDNet) Registry. J Clin Immunol. 2020.
. AT1R Activating Autoantibodies in Hematopoietic Stem Cell Transplantation. Biol Blood Marrow Transplant. 2020.
. Busulfan Pharmacokinetics in ADA SCID Gene Therapy. Biol Blood Marrow Transplant. 2020.
Consensus approach for the management of severe combined immune deficiency caused by adenosine deaminase deficiency. J Allergy Clin Immunol. 2018.
. Gene therapy for blood diseases. Curr Opin Biotechnol. 2018;60:39-45.
. Analyzing CRISPR genome-editing experiments with CRISPResso. Nat Biotechnol. 2016;34(7):695-697.
. Lentivirus Mediated Correction of Artemis-deficient Severe Combined Immunodeficiency. Hum Gene Ther. 2016.
Primary Immune Deficiency Treatment Consortium (PIDTC) update. J Allergy Clin Immunol. 2016.
. Eliminating SCID row: new approaches to SCID. Hematology Am Soc Hematol Educ Program. 2014;2014(1):475-480.
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