Absence of full-length dystrophin impairs normal maturation and contraction of cardiomyocytes derived from human induced pluripotent stem cells. Cardiovasc Res. 2019.
Disease-in-a-Dish: The Contribution of Patient-Specific Induced Pluripotent Stem Cell Technology to Regenerative Rehabilitation. Am J Phys Med Rehabil. 2014..
Gait characteristics in a canine model of X-linked myotubular myopathy. J Neurol Sci. 2014..
Gene replacement rescues severe muscle pathology and prolongs survival in myotubularin-deficient mice and dogs. Ann Transl Med. 2015;3(17):257..
Gene Therapy for Inherited Muscle Diseases: Where Genetics Meets Rehabilitation Medicine. Am J Phys Med Rehabil. 2014;93(11 Suppl 3):S97-S107..
Gene therapy in monogenic congenital myopathies. Methods. 2015..
Guiding Intramuscular Diaphragm Injections Using Real-time Ultrasound & Electromyography. Muscle Nerve. 2014..
Muscle pathology, limb strength, walking gait, respiratory function and neurological impairment establish disease progression in the p.N155K canine model of X-linked myotubular myopathy. Ann Transl Med. 2015;3(18):262..
Use of Adeno-Associated Virus to Enrich Cardiomyocytes Derived from Human Stem Cells. Hum Gene Ther Clin Dev. 2015..