Biblio
CRISPR/Cas9-based disease modelling and functional correction of Interleukin 7 Receptor alpha Severe Combined Immunodeficiency in T-lymphocytes and hematopoietic stem cells. Hum Gene Ther. 2024.
. Hematopoietic stem cell gene editing rescues B cell development in X-linked agammaglobulinemia. J Allergy Clin Immunol. 2024.