Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1. N Engl J Med. 2019;380(16):1525-1534.
Reference Intervals for Lymphocyte Subsets in Preterm and Term Neonates Without Immune Defects. J Allergy Clin Immunol. 2019..
Consensus approach for the management of severe combined immune deficiency caused by adenosine deaminase deficiency. J Allergy Clin Immunol. 2018..
Lentivirus Mediated Correction of Artemis-deficient Severe Combined Immunodeficiency. Hum Gene Ther. 2016.
Primary Immune Deficiency Treatment Consortium (PIDTC) update. J Allergy Clin Immunol. 2016..